ClinPharm Vault
A Phase 2 Study of CDX-0159 in Patients With Chronic Spontaneous Urticaria
Study Snapshot
- Program: Barzolvolimab
- Study ID(s): NCT05368285
- Phase: Phase 2
- Indication: Chronic Spontaneous Urticaria
- Status: Completed
- Sponsor: Celldex Therapeutics
Design
- Study type: INTERVENTIONAL
- Randomization / allocation: RANDOMIZED
- Intervention model: PARALLEL
- Masking: QUADRUPLE
- Primary purpose: TREATMENT
- Enrollment: 208 (ACTUAL)
Population
- Conditions: Chronic Spontaneous Urticaria
- Sex: ALL
- Age range: 18 Years to None
- Healthy volunteers: False
- Summary: The purpose of this study is to assess the clinical effect, the pharmacodynamics, the safety, and the pharmacokinetics of barzolvolimab (CDX-0159) in patients with Chronic Spontaneous Urticaria
Operational design summary
- Arms represented in current CT.gov export: 6
- Active dose regimens represented in current local source layer: 3
- Total study enrollment in CT.gov: 208 (ACTUAL)
- Design interpretation: Placebo-controlled 16-week core with three active barzolvolimab dose regimens, followed by re-randomized active extension reflected in the 6 CT.gov arm groups.
- Per-arm sample size summary: Publication abstract supports placebo-controlled core randomization of 75 mg Q4W (n=53), 150 mg Q4W (n=52), 300 mg Q8W (n=51), and placebo (n=51). The currently generated 52-week CT.gov labels only map cleanly to the sustained 150 mg and 300 mg arms; the re-randomized 75 mg and placebo extension arms remain unresolved at exact row level in the current local evidence layer.
- Arm-size evidence source: PMID 41747871 abstract.
Arms
| Arm | Type | Dose | Frequency | Route | Description | N | Evidence status |
|---|---|---|---|---|---|---|---|
| barzolvolimab 75 mg then 150 mg | EXPERIMENTAL | 75 mg -> 150 mg | Q4W | Subcutaneous | barzolvolimab 75 mg injection subcutaneous every 4 weeks for 16 weeks and then 150 mg injection subcutaneous every 4 weeks for 36 weeks | NR | Summary-level arm-size evidence exists, but exact N is not mapped to this CT.gov arm label in the current local layer |
| barzolvolimab 75 mg then 300 mg | EXPERIMENTAL | 75 mg -> 300 mg | Q4W + Q8W | Subcutaneous | barzolvolimab 75 mg injection subcutaneous every 4 weeks for 16 weeks and then 300 mg injection subcutaneous every 8 weeks for 36 weeks | NR | Summary-level arm-size evidence exists, but exact N is not mapped to this CT.gov arm label in the current local layer |
| barzolvolimab 150 mg | EXPERIMENTAL | 150 mg | Q4W | Subcutaneous | barzolvolimab 150 mg injection subcutaneous every 4 weeks for 52 weeks | 52 | Directly supported by linked local publication/source text or explicit CT.gov arm-level enrollment context |
| barzolvolimab 300 mg | EXPERIMENTAL | 300 mg | Q8W | Subcutaneous | barzolvolimab 300 mg injection subcutaneous every 8 weeks for 52 weeks | 51 | Directly supported by linked local publication/source text or explicit CT.gov arm-level enrollment context |
| Placebo then barzolvolimab 150 mg | EXPERIMENTAL | 150 mg | Q4W | Subcutaneous | Placebo injection subcutaneous every 4 weeks for 16 weeks and then barzolvolimab 150 mg injection subcutaneous every 4 weeks for 36 weeks | NR | Summary-level arm-size evidence exists, but exact N is not mapped to this CT.gov arm label in the current local layer |
| Placebo then barzolvolimab 300 mg | EXPERIMENTAL | 300 mg | Q4W + Q8W | Subcutaneous | Placebo injection subcutaneous every 4 weeks for 16 weeks and then barzolvolimab 300 mg injection subcutaneous every 8 weeks for 36 weeks | NR | Summary-level arm-size evidence exists, but exact N is not mapped to this CT.gov arm label in the current local layer |
Key Efficacy and Safety Findings
- Result status: Published
Efficacy
- Primary endpoint met at week 12 (UAS7 change from baseline, LS mean delta versus placebo): 150 mg Q4W -12.55 (P < 0.0001), 300 mg Q8W -13.41 (P < 0.0001), 75 mg Q4W -6.60 (P = 0.0017).
- Complete response (UAS7 = 0) at week 12: 150 mg 51.1%, 300 mg 37.5%, 75 mg 22.9%, placebo 6.4%.
- Week 52 sustained results (all patients on 150 mg or 300 mg): up to 71% complete response, up to 74% well-controlled disease, with early gains visible from week 1.
- EADV 2025 sponsor poster indicates similarly strong efficacy in low-IgE and normal/high-IgE subgroups at weeks 12 and 52, supporting activity beyond a narrow biomarker-defined subset.
- Week 76 off-treatment follow-up: up to 41% maintained complete response (UAS7 = 0); 69% of Week 52 responders still well-controlled; suggestive of disease modification.
Safety
- Hair color changes (26%), neutropenia (17%), skin hypopigmentation (13%); all mechanism-related, mostly Grade 1, reversible upon discontinuation.
- AEs were not dose-dependent; no association between infections and neutropenia.
- Treatment-related SAEs: 2 (1%) across 156 barzolvolimab-treated patients.
Result source(s)
- PMID 41747871
- raw/sponsors/kit/barzolvolimab/aaaai-2025-csu-poster.md
- raw/sponsors/kit/barzolvolimab/eadv-2024-congress-presentation.md
- raw/sponsors/kit/barzolvolimab/eadv-2025-csu-ige-poster.md
Endpoints
- Primary outcomes:
- Mean change from baseline to Week 12 of UAS7 (Urticaria Activity Score) (time frame: From baseline to Day 85 (Week 12))
Clinical Pharmacology Findings
- PK: ClinicalTrials.gov summary text indicates pharmacokinetics were part of the study objectives or assessments.
- PD: ClinicalTrials.gov summary text indicates pharmacodynamics were part of the study objectives or assessments.
- Linked manuscripts: Primary publication support is available in the registry (PMID 41747871).
Safety Findings
- Safety details should be reviewed in the linked primary publication(s) for fuller interpretation beyond the CT.gov inventory layer.
Linked Evidence
- CT.gov page: https://clinicaltrials.gov/study/NCT05368285
- Local CT.gov cache:
raw/clinicaltrials/markdown/NCT05368285.md - Primary publications:
- PMID 41747871: Randomized dose-finding study of anti-KIT barzolvolimab in patients with chronic spontaneous urticaria. (
../raw/publications/pubmed/markdown/PMID41747871.md)
Interpretation
- Verified facts: this page reflects the current local registry and CT.gov inventory export without inferring unsupported arm sizes or endpoint results.
- Interpretation: this trial already has direct manuscript support in the local source layer and should be a higher-priority candidate for manual enrichment.
- Open questions:
- Some studies still lack exact arm-specific N in the current promoted evidence layer even when allocation schema or total enrollment is visible.
- No sponsor artifact is explicitly linked to this trial by identifier in the current registry.
Provenance
- Source type: ClinicalTrials.gov inventory with linked sponsor/publication registry where available
- Primary source(s):
- NCT05368285
../raw/clinicaltrials/markdown/NCT05368285.md../inventories/source_registry.json- Supporting source(s):
../inventories/ctgov_priority_trials.json- Last verified: 2026-04-08
- Verification status: Partial
Change Log
- 2026-04-08: Generated or refreshed this study page from the v2 source registry and CT.gov inventory.